发明名称 THERAPEUTIC AGENT FOR DUCHENNE MUSCULAR DYSTROPHY
摘要 PROBLEM TO BE SOLVED: To discover a new SES(Splicing Enhancer Sequence) in a dystrophin exon and to obtain a new therapeutic agent for Duchenne muscular dystrophy based on the SES. SOLUTION: This antisense oligonucleotide comprises a base sequence complementary to a base sequence of the formula agcaagaaga cagcagcauu gcaaag or ggaagcuaag gaagaagcug agcagg.
申请公布号 JP2002010790(A) 申请公布日期 2002.01.15
申请号 JP20000348957 申请日期 2000.11.16
申请人 MATSUO MASAFUMI;JCR PHARMACEUTICALS CO LTD 发明人 TAKESHIMA YASUHIRO;MATSUO MASAFUMI
分类号 C12N15/09;A61K9/19;A61K31/7088;A61K47/02;A61K47/04;A61K47/10;A61K47/12;A61K47/14;A61K47/16;A61K47/18;A61K47/26;A61K47/28;A61K48/00;A61P21/00 主分类号 C12N15/09
代理机构 代理人
主权项
地址
您可能感兴趣的专利