发明名称 |
THERAPEUTIC AGENT FOR DUCHENNE MUSCULAR DYSTROPHY |
摘要 |
PROBLEM TO BE SOLVED: To discover a new SES(Splicing Enhancer Sequence) in a dystrophin exon and to obtain a new therapeutic agent for Duchenne muscular dystrophy based on the SES. SOLUTION: This antisense oligonucleotide comprises a base sequence complementary to a base sequence of the formula agcaagaaga cagcagcauu gcaaag or ggaagcuaag gaagaagcug agcagg. |
申请公布号 |
JP2002010790(A) |
申请公布日期 |
2002.01.15 |
申请号 |
JP20000348957 |
申请日期 |
2000.11.16 |
申请人 |
MATSUO MASAFUMI;JCR PHARMACEUTICALS CO LTD |
发明人 |
TAKESHIMA YASUHIRO;MATSUO MASAFUMI |
分类号 |
C12N15/09;A61K9/19;A61K31/7088;A61K47/02;A61K47/04;A61K47/10;A61K47/12;A61K47/14;A61K47/16;A61K47/18;A61K47/26;A61K47/28;A61K48/00;A61P21/00 |
主分类号 |
C12N15/09 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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