发明名称 |
ADENO-ASSOCIATED VIRAL VECTOR-MEDIATED EXPRESSION OF FACTOR VIII ACTIVITY |
摘要 |
The instant invention provides methods and materials for expressing polypeptides with factor VIII activity comprising administering at least two rAAV vectors encoding different domains of human factor VIII and at least the heavy and light chains. |
申请公布号 |
WO9961595(A2) |
申请公布日期 |
1999.12.02 |
申请号 |
WO1999US10472 |
申请日期 |
1999.05.27 |
申请人 |
CELL GENESYS, INC. |
发明人 |
COHEN, LAWRENCE, K.;SPRATT, S., KAYE;COUTO, LINDA |
分类号 |
C12N15/09;A61K35/76;A61K38/43;A61K48/00;A61P7/04;C07K14/755;C12N15/864 |
主分类号 |
C12N15/09 |
代理机构 |
|
代理人 |
|
主权项 |
|
地址 |
|