发明名称 |
PYRAZOLOPYRIDAZINES AND METHODS FOR TREATING RETINAL-DEGENERATIVE DISEASES AND HEARING LOSS ASSOCIATED WITH USHER SYNDROME |
摘要 |
Compounds, compositions and methods for the treatment of retinal degenerative diseases, such as retinitis pigmentosa, Leber's congenital Amaurosis, Syndromic retinal degenerations, age-related macular degeneration and Usher Syndrome, and hearing loss associated with Usher Syndrome are described herein. Usher Syndrome, a rare genetic disorder and a leading cause of deafness and blindness, is associated with a mutation in any one of ten genes. |
申请公布号 |
HK1214180(A1) |
申请公布日期 |
2016.07.22 |
申请号 |
HK20160102422 |
申请日期 |
2016.03.02 |
申请人 |
Usher III Initiative Inc. |
发明人 |
BURLI, Roland Werner;ESMIEU, William Rameshchandra Krishna;LOCK, Christopher James;MALAGU, Karine Fabienne;OWENS, Andrew Pate;HARTE, William Edward |
分类号 |
A61K |
主分类号 |
A61K |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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