发明名称 Compounds for Nonsense Suppression, and Methods for Their Use
摘要 The present invention relates to methods, compounds, and compositions for treating or preventing diseases associated with nonsense mutations in an mRNA by administering the compounds or compositions of the present invention. More particularly, the present invention relates to methods, compounds, and compositions for suppressing premature translation termination associated with a nonsense mutation in an mRNA.
申请公布号 US2016229818(A1) 申请公布日期 2016.08.11
申请号 US201615130318 申请日期 2016.04.15
申请人 PTC Therapeutics, Inc. 发明人 Almstead Neil;Karp Gary M.;Wilde Richard;Welch Ellen;Ren Hongyu
分类号 C07D251/24 主分类号 C07D251/24
代理机构 代理人
主权项
地址 South Plainfield NJ US