发明名称 |
Methods for Treatment of Fabry Disease |
摘要 |
Provided are in vitro and in vivo methods for determining whether a patient with Fabry disease will respond to treatment with a specific pharmacological chaperone. |
申请公布号 |
US2015238474(A1) |
申请公布日期 |
2015.08.27 |
申请号 |
US201514641707 |
申请日期 |
2015.03.09 |
申请人 |
Amicus Therapeutics, Inc. |
发明人 |
Lockhart David;Castelli Jeff |
分类号 |
A61K31/445 |
主分类号 |
A61K31/445 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
Cranbury NJ US |