发明名称 |
METHODS AND ASSAYS FOR FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY |
摘要 |
<p>Provided herein are methods, assays and compositions relating to the treatment of FSHD, particularly by modulating expression of DUX4.</p> |
申请公布号 |
WO2014071340(A1) |
申请公布日期 |
2014.05.08 |
申请号 |
WO2013US68391 |
申请日期 |
2013.11.05 |
申请人 |
UNIVERSITY OF WASHINGTON THROUGH ITS CENTER FOR COMMERCIALIZATION |
发明人 |
MILLER, DANIEL, G.;BLOCK, GREGORY, J. |
分类号 |
C12N5/077;C12N5/02;G01N33/68 |
主分类号 |
C12N5/077 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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