发明名称 METHODS AND ASSAYS FOR FACIOSCAPULOHUMERAL MUSCULAR DYSTROPHY
摘要 <p>Provided herein are methods, assays and compositions relating to the treatment of FSHD, particularly by modulating expression of DUX4.</p>
申请公布号 WO2014071340(A1) 申请公布日期 2014.05.08
申请号 WO2013US68391 申请日期 2013.11.05
申请人 UNIVERSITY OF WASHINGTON THROUGH ITS CENTER FOR COMMERCIALIZATION 发明人 MILLER, DANIEL, G.;BLOCK, GREGORY, J.
分类号 C12N5/077;C12N5/02;G01N33/68 主分类号 C12N5/077
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