发明名称 SPECIFIC MTOR INHIBITORS IN THE TREATMENT OF X-LINKED ADRENOLEUKODYSTROPHY
摘要 The invention relates to novel uses of specific mTOR inhibitors as a medicament, in particular for the treatment of X-linked adrenoleukodystrophy(X- ALD). The invention also relates to a method for identifying a compound potentially useful for the treatment and/or prevention of X-ALD.
申请公布号 WO2016042166(A1) 申请公布日期 2016.03.24
申请号 WO2015EP71563 申请日期 2015.09.21
申请人 FUNDACIÓN DE LA COMUNIDAD VALENCIANA CENTRO DE INVESTIGACIÓN PRÍNCIPE FELIPE;INSTITUT D'INVESTIGACIÓ BIOMÈDICA DE BELLVITGE (IDIBELL);CENTRO DE INVESTIGACIÓN BIOMÉDICA EN RED (CIBER) 发明人 PUJOL ONOFRE, AURORA;KNECHT ROBERTO, ERWIN
分类号 A61K45/06;A61K31/05;A61K31/132;A61K31/138;A61K31/194;A61K31/277;A61K31/341;A61K31/343;A61K31/436;A61K31/451;A61K31/506;A61K31/5415 主分类号 A61K45/06
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