发明名称 |
SPECIFIC MTOR INHIBITORS IN THE TREATMENT OF X-LINKED ADRENOLEUKODYSTROPHY |
摘要 |
The invention relates to novel uses of specific mTOR inhibitors as a medicament, in particular for the treatment of X-linked adrenoleukodystrophy(X- ALD). The invention also relates to a method for identifying a compound potentially useful for the treatment and/or prevention of X-ALD. |
申请公布号 |
WO2016042166(A1) |
申请公布日期 |
2016.03.24 |
申请号 |
WO2015EP71563 |
申请日期 |
2015.09.21 |
申请人 |
FUNDACIÓN DE LA COMUNIDAD VALENCIANA CENTRO DE INVESTIGACIÓN PRÍNCIPE FELIPE;INSTITUT D'INVESTIGACIÓ BIOMÈDICA DE BELLVITGE (IDIBELL);CENTRO DE INVESTIGACIÓN BIOMÉDICA EN RED (CIBER) |
发明人 |
PUJOL ONOFRE, AURORA;KNECHT ROBERTO, ERWIN |
分类号 |
A61K45/06;A61K31/05;A61K31/132;A61K31/138;A61K31/194;A61K31/277;A61K31/341;A61K31/343;A61K31/436;A61K31/451;A61K31/506;A61K31/5415 |
主分类号 |
A61K45/06 |
代理机构 |
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代理人 |
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主权项 |
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地址 |
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