发明名称 ADENO-ASSOCIATED VIRAL VECTOR-MEDIATED DELIVERY OF DNA TO CELLS OF THE LIVER
摘要 The instant invention provides methods of expressing polynucleotides in the cells of the liver comprising administering viral particles comprising a recombinant AAV vector into a mammal, preferably a human.
申请公布号 WO9824479(A1) 申请公布日期 1998.06.11
申请号 WO1997US21398 申请日期 1997.12.02
申请人 SOMATIX THERAPY CORPORATION;UNIVERSITY OF WASHINGTON;SNYDER, RICHARD;DANOS, OLIVIER;COHEN, LAWRENCE;KAY, MARK;THOMPSON, ARTHUR, R. 发明人 SNYDER, RICHARD;DANOS, OLIVIER;COHEN, LAWRENCE;KAY, MARK;THOMPSON, ARTHUR, R.
分类号 A61K38/48;A61K48/00;C12N7/01;C12N15/864;(IPC1-7):A61K48/00;C12Q1/68;C12Q1/70;C12N15/10;C12N15/63;C12N15/86 主分类号 A61K38/48
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