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发明名称
Improved exon skipping compositions for treating muscular dystrophy
摘要
<p>Antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon 53 skipping are described.</p>
申请公布号
AU2013364158(A1)
申请公布日期
2015.07.09
申请号
AU20130364158
申请日期
2013.12.20
申请人
SAREPTA THERAPEUTICS, INC.
发明人
BESTWICK, RICHARD K.;FRANK, DIANE ELIZABETH
分类号
C12N15/113;A61K31/7088
主分类号
C12N15/113
代理机构
代理人
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