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发明名称
METHODS AND COMPOSITIONS FOR TREATING HEMOPHILIA B
摘要
Disclosed herein are methods and compositions for insertion of Factor IX (FIX) sequences into the genome of a cell for treating hemophilia B.
申请公布号
EP2627665(A4)
申请公布日期
2014.02.26
申请号
EP20110833365
申请日期
2011.10.12
申请人
THE CHILDREN'S HOSPITAL OF PHILADELPHIA;SANGAMO BIOSCIENCES, INC.
发明人
GREGORY, PHILIP D.;HIGH, KATHERINE A.;HOLMES, MICHAEL C.;LI, HOJUN
分类号
C07K14/47;A61K31/7088;A61K45/06;A61K48/00;C12N9/64
主分类号
C07K14/47
代理机构
代理人
主权项
地址
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