发明名称 TREATMENT OF FRATAXIN (FXN) RELATED DISEASES BY INHIBITION OF NATURAL ANTISENSE TRANSCRIPT TO FXN
摘要 The present invention relates to antisense oligonucleotides that modulate the expression of and/or function of Frataxin (FXN), in particular, by targeting natural antisense polynucleotides of Frataxin (FXN). The invention also relates to the identification of these antisense oligonucleotides and their use in treating diseases and disorders associated with the expression of FXN.
申请公布号 KR20140033165(A) 申请公布日期 2014.03.17
申请号 KR20137034424 申请日期 2012.06.08
申请人 CURNA, INC. 发明人 COLLARD JOSEPH;KHORKOVA SHERMAN OLGA
分类号 C12N15/113;A61K48/00 主分类号 C12N15/113
代理机构 代理人
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